Fifty years ago, the idea of altering a gene to treat or even cure a disease was considered science fiction. Today, cell and gene therapy are transforming treatment options for some patients and are part of an exciting new era of medicine, noted a Pharmaceutical Research and Manufacturers of America website posting by Andrew Powaleny, director of public affairs at PhRMA.
A new report released today finds there are 289 novel cell and gene therapies in development for a variety of diseases and conditions. The therapies represent the translation of basic scientific insights into innovative new treatment options for patients. These medicines in development are either in clinical trials or awaiting review by the US Food and Drug Administration.
The novel cell and gene therapies in the development pipeline are the result of years of pioneering research. The range of diseases these therapies can address is broad and covers blood and eye disorders, cancer and infectious disease to name a few.
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