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Pharmaceutical
RNA specialist Alnylam Pharmaceuticals (Nasdaq: ALNY) has revealed encouraging topline results from its Phase III HELIOS-B study. 24 June 2024
Biotechnology
The week in pharma: action, reaction and insight – week to June 21, 2024 23 June 2024
Biotechnology
First treatment to address underlying pathophysiology of XLH backed by NICE 21 June 2024
Biotechnology
Expanded US FDA approval of Elevidys in DMD 21 June 2024
Pharmaceutical
Otsuka expands licensing deal for donidalorsen 20 June 2024
Biotechnology
Mirum’s volixibat achieves positive interim analyses 18 June 2024
Biotechnology
Vertex presents positive long-term data on Casgevy at EHA 17 June 2024
Biotechnology
The week in pharma: action, reaction and insight – week to June 14, 2024 16 June 2024
Biotechnology
Shares in both US biopharma Ultragenyx (Nasdaq: RARE) and UK-based Mereo BioPharma (Nasdaq: MREO) closed around 8% higher on Wednesday. 13 June 2024
Biotechnology
Pfizer’s DMD candidate misses Phase III goals 13 June 2024
Biotechnology
US gene therapy company Regenxbio has announced that co-founder Kenneth Mills is to step down as president and chief executive following 15 years of leadership 12 June 2024
Pharmaceutical
Syntis Bio, a new clinical-stage biopharmaceutical company, has officially launched. 11 June 2024
Pharmaceutical
Calico Life Sciences, a biotech company specializing in aging and age-related diseases, has had its candidate fosigotifator accepted into the US Food and Drug A 10 June 2024
Biotechnology
The week in pharma: action, reaction and insight – week to June 7, 2024 9 June 2024
Pharmaceutical
Positive five-year data for Roche’s Evrysdi in SMA 8 June 2024
Pharmaceutical
Abu Dhabi’s Department of Health has signed a Memorandum of Understanding (MoU) with AstraZeneca (LSE: AZN) to establish a world-class Rare Diseases Centre of E 7 June 2024
Biotechnology
Moderna (Nasdaq: MRNA) has announced that the US Food and Drug Administration has selected mRNA-3705 for the Support for Clinical Trials Advancing Rare Disease 6 June 2024
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