Privately-held drugmaker Chiesi has secured approval from the British medicines regulator for Elfabrio (pegunigalsidase alfa) in Fabry disease (FD).
The Italian firm has developed Elfabrio as a long-term enzyme replacement therapy for adults with FD, a serious lysosomal storage disorder which can result in impaired peripheral sensation and organ failure.
Chiesi is working with Israel’s Protalix BioTherapeutics (TASE: PLX) in the development of the therapy, the first and only enzyme replacement therapy of its type in this indication.
This article is accessible to registered users, to continue reading please register for free. A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.
Login to your accountTry before you buy
7 day trial access
Become a subscriber
Or £77 per month
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed
Chairman, Sanofi Aventis UK
Copyright © The Pharma Letter 2024 | Headless Content Management with Blaze