More Chinese trials needed to fill Fabry disease 'treatment gap'

29 September 2023

Information from research group GlobalData suggests there is a pressing need for innovation and collaboration in China to address an unmet medical need in Fabry disease.

Enzyme replacement therapies (ERT) are the current standard of care for people with Fabry disease, an inherited genetic disorder that narrows blood vessels, affecting many parts of the body, including the kidneys and heart.

Options include Sanofi’s (Euronext: SAN) Fabrazyme (agalsidase beta) and Takeda’s (TYO: 4502) Replagal (agalsidase alfa).

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