While excitement about the potential of CRISPR/Cas9 gene editing remains high, a setback for a leading company using this technique shows it is no golden ticket to success.
Stock in Cambridge, USA-based Editas Medicine (Nasdaq: EDIT) dropped a tenth on Thursday and fell a further 4% after hours, after the unveiling of weak results from the Phase I/II BRILLIANCE trial.
Editas is using the study to evaluate its candidate EDIT-101 in the treatment of blindness due to the rare genetic disorder Leber congenital amaurosis 10 (LCA10).
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