The Roche (ROG: SIX) subsidiary Genentech has presented five-year SUNFISH data on Evrysdi (risdiplam) in the final readout of this pivotal study.
These data support the drug’s longer-term efficacy and safety for people with types two and three spinal muscular atrophy (SMA), who are aged two to 25 years at enrollment.
Evrysdi demonstrated long-term stabilization of motor function improvements from baseline that were observed during the first year, as measured by motor function measure 32.
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