Basel’s Roche (ROG: SIX) has announced new exploratory two-year data from the SUNFISH study of Evrysdi (risdiplam) in spinal muscular atrophy (SMA).
The Swiss cancer giant is testing the SMN2 splicing modifier as an option for people with Type 2 or non-ambulant Type 3 SMA.
The data suggests that gains in motor function after the first year are sustained for another 12 months, across primary and secondary endpoint measures.
This article is accessible to registered users, to continue reading please register for free. A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.
Login to your accountTry before you buy
7 day trial access
Become a subscriber
Or £77 per month
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed
Chairman, Sanofi Aventis UK
Copyright © The Pharma Letter 2024 | Headless Content Management with Blaze