NICE provisionally recommends Vimizin (elosulfase alfa) for treatment of Morquio syndrome
The National Institute for Health and Care Excellence (NICE) has provisionally recommended BioMarin’s (NASDAQ: BMRN) Vimizin (elosulfase alfa), it has been announced.
The drug treats mucopolysaccharidosis type IVa (MPS IVa/Morquio A syndrome) – an extremely rare but life-limiting lysosomal storage disease that affects about 88 people in England.
Vimizin is an enzyme replacement therapy consisting of the N-acetylgalactosamine-6-sulfatase enzyme and replaces the enzyme lacking in people with MPS IVa.
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