NICE issues draft guidance backing Galafold for Fabry disease

19 October 2016
amicus-big

USA-based are and orphan disease focussed biotech Amicus Therapeutics (Nasdaq: FOLD) says that the National Institute for Health and Care Excellence (NICE) has issued draft ‘Highly Specialized Technologies’ guidance recommending its Galafold (migalastat) for the treatment of Fabry disease.

The draft guidance from the medicines cost-effectiveness watchdog for England and Wales recommends migalastat only when the company provides it with the confidential discount agreed in the patient access scheme and adds to current approved indications.

With the discount, migalastat provides value for money based on the price of enzyme replacement therapy (ERT), which is the current standard treatment for Fabry disease, the company asserted.

This article is accessible to registered users, to continue reading please register for free.  A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.

Login to your account

Become a subscriber

 

£820

Or £77 per month

Subscribe Now
  • Unfettered access to industry-leading news, commentary and analysis in pharma and biotech.
  • Updates from clinical trials, conferences, M&A, licensing, financing, regulation, patents & legal, executive appointments, commercial strategy and financial results.
  • Daily roundup of key events in pharma and biotech.
  • Monthly in-depth briefings on Boardroom appointments and M&A news.
  • Choose from a cost-effective annual package or a flexible monthly subscription
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed

Chairman, Sanofi Aventis UK

Companies featured in this story

More ones to watch >


Today's issue

Company Spotlight





More Features in Pharmaceutical