A drug to treat a rare inherited bone disorder has been recommended for limited use by Britain’s pricing watchdog after being initially turned down for being too expensive last year.
In draft guidance the National Institute for Health and Care Excellence (NICE) recommended US drugmaker Alexion Pharmaceutical’s (Nasdaq: ALXN) Strensiq (asfotase alfa), which could cost up to £1.5 million ($2 million) per patient per year, for perinatal- and infantile-onset hypophosphatasia (HPP).
Alexion said it welcomed the decision but expressed disappointment that the guidance ‘dismissed’ the needs of children with juvenile-onset HPP.
This article is accessible to registered users, to continue reading please register for free. A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.
Login to your accountTry before you buy
7 day trial access
Become a subscriber
Or £77 per month
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed
Chairman, Sanofi Aventis UK
Copyright © The Pharma Letter 2024 | Headless Content Management with Blaze