Emflaza approval expanded to include younger boys
US pharma PTC Therapeutics (Nasdaq: PTCT) closed 4% up on Friday after announcing an expansion of the labeling for the Duchenne muscular dystrophy (DMD) drug Emflaza (deflazacort) in the USA.
The Food and Drug Administration (FDA) has approved the company’s supplemental New Drug Application to expand its labeling to include patients with DMD who are between two and five-years-old.
Emflaza was first approved by the FDA in February 2017 for the treatment of Duchenne in patients five-years and older.
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