Catalyst Pharmaceutical Partners (Nasdaq: CPRX) and fellow USA-based BioMarin Pharmaceutical (Nasdaq: BMRN) have entered into a strategic collaboration for the rights to Firdapse (amifampridine phosphate) in North America.
Firdapse is an orphan product, which has been approved in the European Union and is undergoing a Phase III clinical trial in the USA, for the treatment of Lambert-Eaton myasthenic syndrome (LEMS), a rare, debilitating and sometimes fatal autoimmune disease with the primary symptoms of muscle weakness. The key components of the collaboration include Catalyst licensing the exclusive North American rights to Firdapse and BioMarin making a $5 million investment in Catalyst to rapidly advance the Firdapse program in the USA.
No current effective LEMS treatment available in USA
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