ProQR Therapeutics

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"ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA medicines."

The firm is focused on the creation of: "transformative RNA medicines for the treatment of severe genetic rare diseases such as Leber’s congenital amaurosis 10, Usher syndrome type 2 and dystrophic epidermolysis bullosa."

The company states: "Based on aunique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind."