Krystal Biotech

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A USA-based company focused on developing and commercializing genetic medicines for patients with rare diseases.

The company’s wide-ranging pipeline is based on its proprietary redosable HSV vector.

In May 2023, Vyjuvek was approved by the US FDA for the treatment of dystrophic epidermolysis bullosa (DEB). Vyjuvek is a non-invasive, topical, redosable gene therapy designed to treat DEB at the molecular level. This made it the first FDA-approved treatment for a rare, devastating skin disease.