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Intellia Therapeutics

A clinical-stage gene editing company focused on revolutionizing medicine with CRISPR-based therapies.

In late 2023, Intellia secured additional financing through a public offering, raising approximately $250 million to support ongoing clinical trials and pipeline expansion.

Intellia is advancing therapies designed to deliver CRISPR/Cas9 components directly into patients to treat genetic diseases at their source. Key programs include NTLA-2001, targeting transthyretin amyloidosis (ATTR), and NTLA-2002, for hereditary angioedema (HAE).

The company is also developing cell-based therapies for hematological cancers and autoimmune diseases, leveraging CRISPR/Cas9 to enhance the functionality of immune cells such as T cells.

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