First hemophilia B patients treated with Hemgenix in Europe

5 July 2024

Global biotechnology firm CSL Behring, part of Australia's CSL Limited (ASX: CSL), has announced that two patients with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene dezaparvovec).

The dosing, which took place at specialist treatment centers in France, marks the first real-world administration of Hemgenix for hemophilia B in Europe.

Senior vice president Lutz Bonacker said: “This milestone has been made possible by the innovative Direct Access scheme adopted in France, allowing patients to benefit from early access to pioneering treatments."

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