uniQure leaps on positive mid-stage data for gene therapy

16 November 2018

Shares in Netherlands-based gene therapy company uniQure (Nasdaq: QURE) jumped over a third in trading on Thursday, after the firm announced positive data from a Phase IIb dose-confirmation study of AMT-061.

The firm is testing the gene therapy for patients with severe and moderately severe hemophilia B.

The data show that therapeutic levels of Factor IX activity were achieved and sustained in all three patients in the trial after six weeks, following a single administration of AMT-061.

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