A new biotech company has been launched with the goal of taking on one of the world’s rarest neurodegenerative diseases.
SynaptixBio is working to develop the world’s first disease-modifying treatment for TUBB4a leukodystrophy, including H-ABC - a debilitating and potentially life-limiting condition.
"We want to ensure that dream becomes a reality"Founded by a worldwide team of leading medical and pharmaceutical experts, the UK-based research company has entered into a sponsored research agreement with Children’s Hospital of Philadelphia (CHOP) in the USA, related to a new method for treating TUBB4a leukodystrophy.
This article is accessible to registered users, to continue reading please register for free. A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.
Login to your accountTry before you buy
7 day trial access
Become a subscriber
Or £77 per month
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed
Chairman, Sanofi Aventis UK
Copyright © The Pharma Letter 2024 | Headless Content Management with Blaze