Spanish genetic medicines company SpliceBio has signed an exclusive collaboration and licensing agreement with Spark Therapeutics, which was acquired by Swiss pharma giant Roche (ROG: SIX) in a $4.8 billion deal in 2020, to utilize SpliceBio’s proprietary Protein Splicing platform to develop a gene therapy for an undisclosed inherited retinal disease.
SpliceBio and Spark will conduct a research collaboration utilizing SpliceBio’s proprietary Protein Splicing platform, which offers the potential to address diseases that currently cannot be treated with gene therapies because the necessary gene is too large to be delivered by adeno-associated virus (AAV) vectors.
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