Scholar Rock continues to build case for entrant into SMA space

25 October 2022

The market for spinal muscular atrophy (SMA), a progressive neuromuscular disease that can be fatal, has attracted many of biopharma’s biggest names.

Biogen’s (Nasdaq: BIIB) Spinraza (nusinersen), Roche’s (ROG: SIX) Evrysdi (risdiplam) and Novartis’ (NOVN: VX) Zolgensma (onasemnogene abeparvovec) are already competing in a market predicted to be worth nearly $2.1 billion by 2026, according to Stratview Research.

But it is not just big pharma players seeking to gain a share of the growing market, with Boston, USA-based biotech Scholar Rock (Nasdaq: SRRK) hopeful of advancing apitegromab, a selective inhibitor of the activation of myostatin which is now being studied in a Phase III study.

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