Sarepta regains momentum as trial hold is lifted

6 September 2022

The US Food and Drug Administration has lifted a clinical hold on research into SRP-5051, a candidate under development by rare disease company Sarepta Therapeutics (Nasdaq: SRPT).

The investigational PPMO therapy is being tested as an option for people with Duchenne muscular dystrophy (DMD) who are amenable to exon 51 skipping.

The hold in Part B of the MOMENTUM study came after a serious adverse event of hypomagnesemia, earlier in the year.

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