Sarepta leaps on positive new mid-stage data with eteplirsen

2 October 2015

US RNA-based drug developer Sarepta Therapeutics (Nasdaq: SRPT) has announced additional clinical efficacy and safety data from the company’s Phase IIb program of eteplirsen in patients with Duchenne muscular dystrophy (DMD).

The data demonstrated that eteplirsen provided a statistically-significant advantage of 151 meters in the ability of study participants to walk at three years, compared with external controls. Further, the fourth biopsy data confirmed the mechanism of action of eteplirsen, demonstrating exon skipping in all patients and dystrophin production in nearly all patients. Safety data remained consistent with prior results.

Sarepta gets Buy rating and $50 per share target

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