Sarepta Therapeutics (Nasdaq: SRPT) has announced it will cease development of SRP-5051, an experimental drug for Duchenne muscular dystrophy, citing safety issues, feedback from the US regulator, and the shifting Duchenne treatment landscape.
The company has reported strong financial results driven by its own Elevidys (delandistrogene moxeparvovec), a recently-approved gene therapy for DMD.
Chief scientific officer Louise Rodino-Klapac said that the company's focus has shifted to therapies with the most robust clinical benefit.
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