Sarepta and GenEdit advance gene therapies for neuromuscular diseases

2 February 2022

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Rare disease specialist Sarepta Therapeutics (Nasdaq: SRPT) and genetic medicine company GenEdit are expanding an agreement to develop gene editing therapeutics for the treatment of neuromuscular diseases.

The collaboration will leverage GenEdit’s proprietary NanoGalaxy polymer nanoparticle platform for tissue-selective delivery.

Sarepta will gain exclusive option rights to license polymer nanoparticles developed by GenEdit in the collaboration, for up to four neuromuscular indications selected by Sarepta.

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