Sangamo gets fast track designation for hemophilia candidate

17 May 2017

Days after revealing a potential half-billion dollar collaboration in hemophilia with Pfizer (NYSE: PFE), US gene editing specialist Sangamo Therapeutics (Nasdaq: SGMO) announced that the US regulator has granted Fast Track designation to SB-525.

The company’s gene therapy candidate for hemophilia A, which forms part of the exclusive, global deal with Pfizer, is designed to deliver a synthetic, liver-specific promoter with a single infusion.

The decision means the company will have more frequent communication with the US Food and Drug Administration, which has also designated the therapy an Orphan Drug, in order to expedite the review process.

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