PTC deals a blow to Biogen in SMA

19 June 2018

PTC Therapeutics (Nasdaq: PTCT) saw its share price rise sharply over the weekend, following the revealing of encouraging data regarding the company's spinal muscular atrophy (SMA) treatment risdiplam.

The Phase I data, from the FIREFISH trial, showed significant improvements to more than 90% of babies within 184 days of commencing treatment with risdiplam. The results were presented at the 22nd annual SMA Researcher Meeting.

Stuart Peltz, chief executive of PTC Therapeutics, said: "The survival data and CHOP-INTEND scores are very promising, since babies with Type 1 SMA typically do not experience functional motor milestone improvement based on natural history. We look forward to sharing updates for the programs as the data further develop at upcoming medical meetings."

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