Positive FDA discussion lifts Rocket amid $175 million funding round
Stock in New Jersey, USA-based Rocket Pharmaceuticals (Nasdaq: RCKT) shot up around 40% on Wednesday, following good news on the financing and regulatory fronts.
Rocket is working on genetic therapies for rare childhood disorders with high unmet need, following a platform-agnostic approach to target different indications.
The company announced on Tuesday that “alignment has been reached” with the US regulator on a pivotal Phase II trial for its lead candidate RP-A501, in the fatal genetic disorder Danon disease.
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