The UK’s National Institute for Health and Care Excellence (NICE) has recommended Biogen’s (Nasdaq: BIIB) Spinraza (nusinersen) to treat infants, children and adults with spinal muscular atrophy (SMA).
It will be the first ever treatment for children with the rare muscle-wasting condition funded by National Health Service (NHS) England.
The NICE’s evaluation of Spinraza was based on the largest body of clinical evidence currently available across all types of SMA, with six years of data relating to more than 300 patients treated who had pre-symptomatic, infantile (type I) and later-onset (types II and III) SMA.
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