Orchard Therapeutics, a new biotech with operations in the UK and USA, has officially launched its mission to save children’s lives by advancing gene therapies thanks to funding of $30 million from venture backers F-Prime Capital.
As part of its launch, the company has announced formal partnerships with a series of academic institutions on both sides of the Atlantic. These are University College London (UCL), Great Ormond Street Hospital for Children NHS Foundation Trust (GOSH), the University of Manchester, the University of California Los Angeles and Boston Children’s Hospital. They have come together with the aim of developing transformative gene therapies for serious and life-threatening orphan diseases.
Orchard’s development programs exploit the potential of ex-vivo autologous hematopoietic stem cell gene therapy to restore normal gene function in primary immune deficiencies, metabolic diseases and hematological disorders.
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