Australian biotech Neuren Pharmaceuticals (ASX: NEU) saw its share jump more than 22% to A$29.5 today, after it announced top-line results from its Phase II clinical trial of NNZ-2591 in children with Phelan-McDermid syndrome (PMS).
Significant improvement was observed by both clinicians and caregivers from treatment, across multiple efficacy measures, said Neuren. Improvements were consistently seen across many of the core PMS characteristics. PMS has severe quality of life impacts for those living with the syndrome, as well as parents and siblings.
According to the company, there are no approved treatments for PMS despite its severely debilitating impact.
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