Mustang Bio (Nasdaq: MBIO) has been awarded Rare Pediatric Disease designation for MB-207 from the US Food and Drug Administration.
The firm is focused on cell and gene therapies to treat hematologic cancers, solid tumors and rare genetic diseases.
MB-207 is a lentiviral gene therapy for the treatment of certain people with X-linked severe combined immunodeficiency (XSCID), also known as bubble boy disease.
The firm, which already received the designation for people with newly diagnosed XSCID, is also developing MB-207 for people who have been treated with a hematopoietic stem cell transplantation (HSCT), without success.
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