Gene therapy specialist takes aim at Duchenne muscular dystrophy

7 January 2021
2020_biotech_lab_vial_research_big

In a wide-ranging clinical update, East Coast, USA-based gene therapy firm Regenxbio (Nasdaq: RGNX) announced that its pivotal trial program for RGX-314 in wet AMD is now active.

The firm also announced a new program, RGX-202, a novel, potentially best-in-class, one-time gene therapy for the treatment of Duchenne muscular dystrophy (DMD).

Wet AMD

This article is accessible to registered users, to continue reading please register for free.  A free trial will give you access to exclusive features, interviews, round-ups and commentary from the sharpest minds in the pharmaceutical and biotechnology space for a week. If you are already a registered user please login. If your trial has come to an end, you can subscribe here.

Login to your account

Become a subscriber

 

£820

Or £77 per month

Subscribe Now
  • Unfettered access to industry-leading news, commentary and analysis in pharma and biotech.
  • Updates from clinical trials, conferences, M&A, licensing, financing, regulation, patents & legal, executive appointments, commercial strategy and financial results.
  • Daily roundup of key events in pharma and biotech.
  • Monthly in-depth briefings on Boardroom appointments and M&A news.
  • Choose from a cost-effective annual package or a flexible monthly subscription
The Pharma Letter is an extremely useful and valuable Life Sciences service that brings together a daily update on performance people and products. It’s part of the key information for keeping me informed

Chairman, Sanofi Aventis UK

Companies featured in this story

More ones to watch >


Today's issue

Company Spotlight





More Features in Biotechnology