Gene therapy specialist takes aim at Duchenne muscular dystrophy
In a wide-ranging clinical update, East Coast, USA-based gene therapy firm Regenxbio (Nasdaq: RGNX) announced that its pivotal trial program for RGX-314 in wet AMD is now active.
The firm also announced a new program, RGX-202, a novel, potentially best-in-class, one-time gene therapy for the treatment of Duchenne muscular dystrophy (DMD).
Wet AMD
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