FDA considers smaller group for Sarepta gene therapy approval

25 May 2023

Sarepta Therapeutics (Nasdaq: SRPT) closed 11% lower following Wednesday’s trading.

The genetic medicine company had provided markets with an update on the Biologics License Application (BLA) for SRP-9001 (delandistrogene moxeparvovec).

This gene therapy is currently under review for the treatment of ambulant individuals with Duchenne muscular dystrophy (DMD) who have a confirmed mutation of the DMD gene.

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