EMA recommends ending authorization of PTC's Translarna

18 September 2023

The European Medicines Agency (EMA) has recommended not renewing the marketing authorization for Translarna (ataluren).

PTC Therapeutics’ (Nasdaq: PTCT) drug is used for treating patients with Duchenne muscular dystrophy whose disease is caused by a type of genetic defect called a ‘nonsense mutation’ in the dystrophin gene and who are able to walk.

PTC shares slide

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