Early results strengthen Sarepta's hand in DMD
US RNA-based drug developer Sarepta Therapeutics (Nasdaq: SRPT) is still climbing even after closing 14% up on Wednesday, at $46.73.
The reason for the sudden share activity this time was not related to Exondys 51 (eteplirsen), the company’s approved treatment for Duchenne muscular dystrophy (DMD), which the US Food and Drug Administration (FDA) gave the nod to last year, ignoring expert views and a mixed data set and arguing that the lack of treatment options for the muscle-wasting disease made the approval justified.
"These data further validate the broad application of our exon-skipping platform"
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