CSL Behring remains confident in Hemgenix despite NICE rejection

2 August 2023

The UK's National Institute for Health and Care Excellence (NICE) has issued a draft Appraisal Consultation Document recommending against CSL Behring’s Hemgenix (etranacogene dezaparvovec) for severe and moderately severe hemophilia B (congenital factor IX deficiency) patients without a history of Factor IX (FIX) inhibitors.

As a result of the initial recommendation, Hemgenix will not be reimbursed by National Health Service (NHS) England as the first and only single infusion gene therapy treatment for adults with the condition.

Despite this, CSL Behring says that it remains confident in the potential benefits of its medicine for eligible patients, and its potential long-term value for the NHS.

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