Boy dies in Pfizer DMD trial

8 May 2024

US pharma giant Pfizer (NYSE: PFE) shared some sad clinical trial news Tuesday.

The company disclosed that a boy taking part in the Phase II DAYLIGHT study for Duchenne muscular dystrophy (DMD) had died suddenly.

"The patient received the investigational gene therapy, fordadistrogene movaparvovec, in early 2023"This study is evaluating the safety and dystrophin expression of fordadistrogene movaparvovec, Pfizer’s gene therapy candidate for DMD, in boys who are two and three years old.

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