BioMarin bags Brineura nod for broader patient population

25 July 2024

Californian drugmaker BioMarin Pharmaceutical (Nasdaq: BMRN) has announced that the US Food and Drug Administration has approved a label expansion for Brineura (cerliponase alfa).

This approval broadens the approved uses of Brineura to include children of all ages with neuronal ceroid lipofuscinosis type 2 (CLN2 disease), regardless of symptoms.

Previously, Brineura was approved for symptomatic children aged three and older with late infantile CLN2 disease.

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