RNAi specialist Alnylam Therapeutics’ (Nasdaq: ALNY) Amvuttra (vutrisiran) has been recommended for use on the National Health Service (NHS) in England as an option for treating hereditary transthyretin-related (ATTRv) amyloidosis.
The RNAi therapeutic is one of the first rare disease medicines to receive a positive draft recommendation under a streamlined pilot process from the National Institute for Health and Care Excellence (NICE) that aims to expedite patient access to promising new treatments.
Amvuttra is a subcutaneous injection administered once every three months that seeks to address the root cause of ATTRv amyloidosis by reducing the production of the abnormal protein that drives this disease.
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