Size of task in rare disease space laid before industry and partners

10 November 2021

More than 90% of the approved identified rare diseases lack an approved treatment option.

That was the challenge set out for European Union health policymakers, drugmakers and the rest of the rare diseases community at a conference on Tuesday.

The event, entitled European Rare Diseases Ecosystem: A Collaborative Path Forward, was sponsored by Alexion, a specialist biotech that has recently been acquired by Anglo-Swedish pharma major AstraZeneca (LSE: AZN).

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